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Rare Diseases
Latest News & Journal Articles View All
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AlertFDA Approves Orphan Drug Evinacumab-dgnb for Homozygous FH
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Beyond COVID-19: Can mRNA Treat Diseases, Too?
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AlertFDA Grants MET Inhibitor Tepotinib Accelerated Approval for NSCLC
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COVID-19 Virus May Prompt Body to Attack Itself
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Meta-Analysis Finds Much Less Lupus Than Expected
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Consensus on Diagnosis, Management of Acute Flaccid Myelitis
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AlertFDA Approves First and Only Treatment for AL Amyloidosis
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Alexion Pauses Enrollment for COVID-19 Study Testing Its Rare Blood-Disorder Drug