Medscape Medical News

Alert FDA Approves Avacopan for Rare ANCA Autoimmune Disease ChemoCentryx said it plans to price its new medicine at an annual cost of $150,000 to $200,000 for US patients.
News, October 08, 2021
Alert FDA Approves Orphan Drug Evinacumab-dgnb for Homozygous FH Indicated for homozygous familial hypercholesterolemia on top of other lipid-modifying therapy, Evkeeza (Regeneron) is a first-in-class inhibitor of a protein involved in lipid metabolism.
News, February 11, 2021
Alert FDA Clears Adalimumab (Humira) for Hidradenitis Suppurativa The TNF blocker becomes the first and only FDA-approved agent for treatment of moderate to severe hidradenitis suppurativa.
News, September 11, 2015
Alert CHMP Backs Antifungal Isavuconazole (Cresemba) The triazole antifungal is indicated for treatment of adults with invasive aspergillosis and mucormycosis in patients for whom amphotericin B is not appropriate.
News, July 29, 2015
Alert FDA Approves New Antifungal Cresemba Indicated to treat the rare infections mucormycosis and aspergillosis, the drug received priority review and extended patent protection.
News, March 06, 2015
Alert Multiple Myeloma Compound Gets Orphan Drug Status KRN5500 is a spicamycin derivative that exhibits antimyeloma effects by impairing both myeloma cells and osteoclasts.
News, June 17, 2014
Alert Vintafolide for Resistant Ovarian Cancer Okayed in Europe A targeted therapy for a subgroup of ovarian cancer patients, plus diagnostic tests to identify these patients, has been recommended for approval.
News, March 21, 2014
Alert FDA Grants Orphan Drug Status to Gevokizumab The FDA has granted orphan drug designation to gevokizumab for the treatment of noninfectious intermediate uveitis, posterior uveitis, or panuveitis, or chronic noninfectious anterior uveitis.
News, August 29, 2012
Alert Hemophilia B Gene Therapy Receives Orphan Status in US A promising gene therapy for hemophilia B has received orphan designation from the US Food and Drug Administration.
News, January 05, 2012

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